Taldefgrobep alfa did not significantly improve motor function across the total population of treated spinal muscular atrophy ...

Years after losing a child to SMA, columnist Helen Baldwin shares that she has many blessings to be thankful for — courtesy of the disease.

Liver-specific SMN1 gene therapy both improved liver functioning, and also reduced other SMA-like symptoms in a mouse model ...

Recent progress in SMA research and advocacy was celebrated at Cure SMA's annual Hope on the Hill event in Washington, D.C.

More than half of SMA patients in an Australian survey said they did not notice any improvement in their symptoms following ...

Columnist Kevin Schaefer feels adulthood with SMA is like a "Star Trek" mission: to boldly go into uncharted territory.

Individually and collectively, it’s vital to be sensitive to what’s happening in the world around us. This awareness allows ...

SMA treatment Spinraza followed by Zolgensma improved motor function and prevented worsening of breathing difficulties in a ...

Since her SMA assignment, columnist Helen Baldwin has learned to look for the bright spots — even in Hurricane Helene's ...

Advanced genetic testing helped clinicians identify novel SMN1 mutations in two children in China, and correctly diagnose ...

Living with spinal muscular atrophy (SMA) often means facing many hardships and uncertainties. With physical limitations, emotional hurdles, and complex medical issues, SMA is constantly shaping and ...